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ASGCT 2026: GS-100 Gene Therapy Demonstrates Early Activity in NGLY1 Deficiency
New interim ASGCT 2026 findings suggest investigational AAV9 gene therapy GS-100 may improve motor and cognitive outcomes in children with NGLY1 Deficiency, while informing dose optimization and immune management strategies.
- Published by
- CGTLive
- Evidence type
- Laboratory
New interim ASGCT 2026 findings suggest investigational AAV9 gene therapy GS-100 may improve motor and cognitive outcomes in children with NGLY1 Deficiency, while informing dose optimization and immune management strategies.
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