1. Strategies for overcoming extracellular and intracellular delivery barriers in Liver-Targeted gene therapy
Yang J, Zhang J, Jiang J, Liang G, Li Z
Liver-targeted gene therapy holds great potential for treating diverse hepatic disorders, yet its efficacy is significantly hindered by complex extracellular and intracellular delivery barriers. This review systematically delineates the pathophysiological obstacles that impede the efficient delivery of nucleic acid…
- Extracellular barriers
- Intracellular barriers
- Liver diseases
- Liver-targetedgene therapy
- Non-viral vectors
