Molecular medicine reports2026ReviewNon-viral Gene Delivery
1. Gene therapy for epilepsy: From SCN1A to broadened therapeutic horizons (Review)
Qin R, Hu X, Jiang W, Wang J, Zheng M, Zhang Z, Et Al.
Genetic epilepsy, for which the molecular mechanisms are relatively well defined in numerous monogenic forms, represents an attractive model for the transition from symptomatic seizure control to mechanism‑driven correction. However, gene therapy strategies differ in their mechanisms of action, adaptability to…
- Dravet syndrome
- adeno‑associated virus
- antisense oligonucleotide
- epilepsy
- gene therapy
- lipid nanoparticles
